Tag Archives: gene therapy

Knock down of BCL11A

There is great excitement in the sickle cell world at the moment about, what may turn out to be, a turning point in the the long road to find a practicable cure for sickle cell. A recent paper from the … Continue reading

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Research interest and funding in sickle cell

The autumn has brought a rush of new publications on sickle cell disease and the 9th Sickle Cell & Thalassaemia Conference, organised by Dr Baba Inusa from Guy’s & St Thomas’ Hospital (7th to 9th October 2015), clarified many of … Continue reading

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Gene Therapy

There is a growing interest in the medical world in gene therapy, for patients who have an inherited disease due to a single gene defect. Sickle cell disease fits this bill perfectly. The condition is caused by a mutation, or … Continue reading

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