Category Archives: gene therapy

Knock down of BCL11A

There is great excitement in the sickle cell world at the moment about, what may turn out to be, a turning point in the the long road to find a practicable cure for sickle cell. A recent paper from the … Continue reading

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Research interest and funding in sickle cell

The autumn has brought a rush of new publications on sickle cell disease and the 9th Sickle Cell & Thalassaemia Conference, organised by Dr Baba Inusa from Guy’s & St Thomas’ Hospital (7th to 9th October 2015), clarified many of … Continue reading

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More on Gene Therapy

In November last year (Gene Therapy: 03/11/14) I discussed the topic of gene therapy and noted that this novel form of treatment was on the cusp of moving from the laboratory into the clinic. At that time, gene therapy involved … Continue reading

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Gene Therapy

There is a growing interest in the medical world in gene therapy, for patients who have an inherited disease due to a single gene defect. Sickle cell disease fits this bill perfectly. The condition is caused by a mutation, or … Continue reading

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